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Data · dataset · 2026

Niemann-Pick disease type C1: 24(S)-hydroxycholesterol pre/post adrabetadex

Listed in Teesside University Research Data Repository

Cerebrospinal fluid 24(S)hydroxycholesterol levels pre and post (48 hr) administration of intrathecal adrabetadex/VTS270?HPBCD in individuals with Niemann-Pick disease type C1

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Catalogue records · 1

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Inferred from text
Disease 75%
Provenance · 1 source records, 12 field assertions
SourceKeyLast seenRaw
Teesside University Research Data Repositoryoai:data.mendeley.com/xccvwtr3f2.110 d agoJSON v1
FieldAssertionExtractorEvidence
access_levelsource · researchdata tees ac ukconnector:researchdata_tees_ac_uk@1.0.0
concepts[disease].local:disease:diseaseenrichment · researchdata tees ac ukkeyword-concept-rules@1.0.0title+description (75%)
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concepts[field].local:field:humanitiesmapping · researchdata tees ac ukconnector:researchdata_tees_ac_uk@1.0.0
concepts[field].local:field:life-sciencesmapping · researchdata tees ac ukconnector:researchdata_tees_ac_uk@1.0.0
concepts[field].local:field:medicine-healthmapping · researchdata tees ac ukconnector:researchdata_tees_ac_uk@1.0.0
concepts[field].local:field:social-sciencemapping · researchdata tees ac ukconnector:researchdata_tees_ac_uk@1.0.0
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