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Data · dataset · 2026

Avalglucosidase alfa-ngpt

Listed in Virginia Open Data Portal

Nexviazyme (avalglucosidase alfa-ngpt) is an enzyme replacement therapy used to treat Pompe disease, a rare genetic disorder causing muscle weakness.

Description

It's administered intravenously as a powder for solution, with each vial containing 100 mg of the active ingredient. Manufactured by Genzyme Corporation, it's approved for prescription use.

This information was generated using AI and is provided for informational and research purposes only.

Links

Documentation and papers

Catalogue records · 1

Topics

Inferred from text
Disease 75%
Provenance · 1 source records, 8 field assertions
SourceKeyLast seenRaw
Virginia Open Data Portal138a9443-4e73-4ddd-9605-09585292aeb49 h agoJSON v1
FieldAssertionExtractorEvidence
concepts[disease].local:disease:diseaseenrichment · data virginia govkeyword-concept-rules@1.0.0title+description (75%)
concepts[field].local:field:engineeringmapping · data virginia govconnector:data_virginia_gov@1.0.0
concepts[field].local:field:medicine-healthmapping · data virginia govconnector:data_virginia_gov@1.0.0
created_datesource · data virginia govconnector:data_virginia_gov@1.0.0
descriptionsource · data virginia govconnector:data_virginia_gov@1.0.0/notes
publication_datesource · data virginia govconnector:data_virginia_gov@1.0.0
titlesource · data virginia govconnector:data_virginia_gov@1.0.0/title
updated_datesource · data virginia govconnector:data_virginia_gov@1.0.0