Data · dataset · 2026
Avalglucosidase alfa-ngpt
Listed in Virginia Open Data Portal
Nexviazyme (avalglucosidase alfa-ngpt) is an enzyme replacement therapy used to treat Pompe disease, a rare genetic disorder causing muscle weakness.
Description
It's administered intravenously as a powder for solution, with each vial containing 100 mg of the active ingredient. Manufactured by Genzyme Corporation, it's approved for prescription use.
This information was generated using AI and is provided for informational and research purposes only.
Links
Get the data
- Avalglucosidase alfa-ngpt accessdata.fda.gov/scripts/cder/daf/index.cfm?event=overview.process&ApplNo=761194 ↗
download · from data virginia gov
Where it is published
- Virginia Open Data Portal dataset page data.virginia.gov/dataset/avalglucosidase-alfa-ngpt1 ↗
landing page · from data virginia gov
Documentation and papers
- Publisher page fda.gov/drugs ↗
documentation · from data virginia gov
Catalogue records · 1
- CKAN API data.virginia.gov/api/3/action/package_show?id=138a9443-4e73-4ddd-9605-09585292a… ↗
metadata API · from data virginia gov
Topics
- From keywords
- Engineering · Medicine & Health
- Inferred from text
- Disease 75%
Provenance · 1 source records, 8 field assertions
| Source | Key | Last seen | Raw |
|---|---|---|---|
| Virginia Open Data Portal | 138a9443-4e73-4ddd-9605-09585292aeb4 | 9 h ago | JSON v1 |
| Field | Assertion | Extractor | Evidence |
|---|---|---|---|
| concepts[disease].local:disease:disease | enrichment · data virginia gov | keyword-concept-rules@1.0.0 | title+description (75%) |
| concepts[field].local:field:engineering | mapping · data virginia gov | connector:data_virginia_gov@1.0.0 | |
| concepts[field].local:field:medicine-health | mapping · data virginia gov | connector:data_virginia_gov@1.0.0 | |
| created_date | source · data virginia gov | connector:data_virginia_gov@1.0.0 | |
| description | source · data virginia gov | connector:data_virginia_gov@1.0.0 | /notes |
| publication_date | source · data virginia gov | connector:data_virginia_gov@1.0.0 | |
| title | source · data virginia gov | connector:data_virginia_gov@1.0.0 | /title |
| updated_date | source · data virginia gov | connector:data_virginia_gov@1.0.0 |