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Data · dataset · 2026

A Study to Explore the Safety, Tolerability, Pharmacokinetic Profile, and Potential Efficacy of Guanabenz in Patients With Early Childhood Onset Vanishing White Matter (VWM)

Listed in IISH Dataverse

This clinical trial dataset comprises data from 33 patients with Vanishing White Matter who are treated with Guanabenz.

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Where it is published

Catalogue records · 1

Topics

Provenance · 1 source records, 9 field assertions
SourceKeyLast seenRaw
IISH Dataversedoi:10.34894/4I9UPP11 d agoJSON v1
FieldAssertionExtractorEvidence
concepts[field].dataverse_subject:medicine-health-and-life-sciencessource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0/subjects
concepts[field].local:field:life-sciencesmapping · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0/subjects
concepts[field].local:field:medicine-healthmapping · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0/subjects
created_datesource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0
descriptionsource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0/description
publication_datesource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0
titlesource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0/name
updated_datesource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0
version_labelsource · datasets iisg amsterdamconnector:datasets_iisg_amsterdam@1.0.0